Business Development + Partnering

Industry Sponsored Clinical Trials

Below is a list of ongoing and past industry initiated and sponsored clinical trials at Children’s Hospital Boston. (Click on the boxes to expand.)

2008

open

Principle Investigator Study Title Sponsor
Rosalind Brown Genotropin/Growth Hormone Pfizer, Inc.
Sarah DeFerranti Hypertriglyceridemia in Children United Biosciences Corporation
Maureen Jonas Entecavir Evaluation in children with HBV Bristol Myers Squibb
Wanda Phipatanakul Buffalo Milk/Children with Dairy Allergies The Woodstock Water Buffalo Company
Ellis Neufeld Registry/Hematology Novartis
Athos Bousvaros Adalimumbab Double Blind Abbott Labs
Rosalind Brown rhIGF-1/Growth Hormone Tercica
Mary McCann SEDLine and BIS/Anesthesia Hospira
Cami Martin Aztreonam/Pulmonary Gilead Sciences, Inc.
Adrienne Randolph Lucinactant in Acute Hypoxemic Respiratory Failure Discovery Labs
Ellis Neufeld AMG 531/Hematology Amgen Inc.
Debbie Chirnomas Inadequate Response to Exjade/Hematology Novartis
Wenn-Han Tan Betaine Angelman/Genetics Rare Disease Therapeutics
Blaise Bourgeois Rufininide II/Neurophysiology Eisai, Inc.
Robert Geggel BioSignetics Software Development/Cardiology BioSignetics Corporation
Joseph Gonzalez-Heydrich Open label Paliperidone/Psychiatry Johnson & Johnson
Joseph Gonzalez-Heydrich Double blind Paliperidone/Psychiatry Johnson & Johnson
Greg Sawicki Liposomal Amikacin for Inhalation in CF Patients with Chronic Infections Due to Pseudomas Aeruginosa Transave
Francis Fynn-Thompson Berlin Heart/Cardiology Berlin Heart
Rosalind Brown Norditropin National Registry/Endocrinology Novo Nordisk
Ellis Neufeld GA-GCB Enzyme Replacement Therapy Shire Human Genetic Therapies
John Goldberg ARQ197/Hematology Arqule
Kathy Jenkins COAST/Cardiology Johns Hopkins University
Audrey Marshall COAST/Cardiology Johns Hopkins University
Stavroula Osganian Omacor/Obesity Reliant/GlaxoSmithKline
Rosalind Brown MS316/Growth Hormone Tercica
Ellis Neufeld Novo Seven/Hematology Novo Nordisk
Edward Neilan Protocol Development Stage of Prodarsan Study/Genetics Pharming Healthcare, Inc./Dnage
Ellis Neufeld NN1731-1804/Hematology Novo Nordisk
Terry Spencer TIGER-2/Pulmonary Inspire Pharmaceuticals, Inc.
Terry Spencer MPEX 204/Pulmonary Mpex Pharmaceuticals
Basil Darras PTC 124/Neurology PTC Therapeutics, Inc.
Terry Spencer Safety of ALTU-135 Treatment/Pulmonary Altus Pharmaceuticals
Blaise Bourgeois Levetiracetam Intravenous Infusion/Neurophysiology UCB Pharma
Ellis Neufeld Dosing Observational Study/Hematology Novo Nordisk
Athos Bousvaros Gardasil HPB Vaccine & GI Merck & Co., Inc.
Ahmet Uluer Bayer 12429/Pulmonary Bayer Group
William Harmon Belatacept CD80 CD86/Nephrology Bristol Myers Squibb
Terry Spencer Trial of Azithromycin in CF Patients/Pulmonary Cystic Fibrosis Foundation
Lynda Schneider Change 2 Open Label/Dermatology LEV Pharmaceuticals
Debbie Chirnomas Ferriprox (Deferiprone) Expanded Access/ Hematology ApoPharma, Inc.
Karen Marcus Profiling DNA Repair Pathways DNAR, Inc.

2007

open
Principle Investigator Study Title Sponsor
Sandra Burchett TMC114/rtv in Experienced HIV-1 Infected Children Tibotec Pharmaceuticals Ltd.
Susan Kim Study to Evaluate the Efficacy and Safety of Rituximab in Subjects with ISN/RPS Class III or IV Lupus Nephritis Genentech
Eva Guinan Defibrotide for Treatment of Severe Hepatic VOD in HSCT Patient Gentium SpA
Deborah Weiner Role of Nitric Oxide of White Blood Cell Function in Inflammation and Infection University of Washington
Joseph Borer Study of Augmentation Cystoplasty Tengion, Inc.
Eva Guinan Opebacan in Patients Undergoing Myeloablative Allogeneic hematopoietic Stem Cell Transplantation XOMA Ltd.
James Lock Transcatheter/Cardiac Study Medtronic, Inc.
Paul Rufo Phase I/II Trial of Topical Clotrimaxole in Pediatric and Adult Patients with Pouchitis Effective Pharmaceuticals
Kirsten Ecklund IDEAL/MRI Capability Study General Electric
Jonathan Mansbach Lower Respiatory Tract/Chart Review AstraZeneca
Michael Landzberg COMPASS II/Cardiac Actelion
Sam Nurko Lubiprostone/GI Sucampo Pharmaceuticals, Inc.
Sam Nurko Lansoprazole/GI TAP Pharmaceutical Products Inc.
Cami Martin Prochieve Beth Israel Deaconess Medical Center
Anne Fulton Vigabatrin Ovation Pharmaceuticals Inc.
Blaise Bourgeois Rufinamide Eisai
Kieran Gulati Progeria Disease Schering-Plough Corporation
Charles Berul Cardioverter-Defibrillators: A Proscpective Study Yale University
Francisco Bonilla Subcutaneous Gamunex 10% in Subjects with Primary Immunodeficiencies Talecris Biotherapeutics
Mark Proctor Durepair Dura Regeneration Matrix Medtronic, Inc.
Kristin Odegard CLARINET/Congenital Heart Disease Sanofi-Aventis/Bristol Myers Squibb
Manali Amin Effects of Gastro-Esophageal Acid Surpression… TAP Pharmaceutical Products Inc.
Harpreet Pall Registry for Studies of Primary Sclerosing Cholangitis (STOPSC) Emmes/Morgan Foundation
Michael Landzberg COMPASS III/Cardiology Actelion
Joseph Gonzalez-Heydrich Psychiatry Pfizer, Inc.
Joseph Gonzalez-Heydrich Psychiatry Pfizer, Inc.
Ahmet Uluer Tiotropium Bromide/Pulmonary Boehringer Ingelheim
Sam Nurko Pantoprazole and GERD/GI Wyeth
Audrey Marshall SALSA/Cardiology NMT Medical, Inc.
Ahmet Uluer VX-770/Pulmonary Vertex Pharmaceuticals
Suzanne Shusterman Pilot Study of Tandem High Dose Chemotherapy with Stem Cell Rescue… University of Pennsylvania
Michael Landzberg ARIES 3/Cardiology Gilead Sciences, Inc.
Ellis Neufeld Subcontract ZLB/Hemotology Emory University
Joseph Madsen CFS/Neurology Neuro Diagnostics Devices
Harvey L. Levy Expanded Access/ Phenylketonuria BioMarin Pharmaceutical, Inc.

2006

open
Principle Investigator Study Title Sponsor
Deborah Marsden PKU Using the Medical Food Lophlex SHS International
Ellis Neufeld A Retrospective Study to Capture Dosing and Treatment Outcome Data in Subjects with Severe Congenital Protein C Defict Baxter Healthcare
Roger Breitbart A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Immunogenicity of MEDI-524 in Children MedImmune
Lynda Schneider C1 Esterase Inhibitor ZLB Behring
Jonathan Mansbach Frequency of Human Metapneumovirus and Respiratory Syncytial Virus in Bronchiolitis Massachusetts General Hospital
Ellis Neufeld Incidence of Inhibitor Formulation in Hemophilia A patients ZLB Behring
Leslie Smoot Expanded Aaccess Use of Recombinant Human Acid a-Glucose (rhGAA) (Myozyme) in Patients with Infantile-Onset Pompe Disease. Genzyme Corporation
Lyle Micheli Prospective Study to Evaluate the Effectiveness of Adjunctive Genzyme Corporation
Ellis Neufeld IND for Protein C Baxter Healthcare
Blaise Bourgeois Safety and Efficacy of Clobazam in Subjects with Lennox-Gastaut Syndrome Ovation Pharmaceuticals Inc.
Kathy Jenkins Plavis Clopidogrel Usage in Pediatric Population at CH Bristol Myers Squibb
Harmon, William Trial of Steroid Withdrawal in Sirolimus and Cyclosporine-Treated Primary Transplant Recipients Wyeth
Thomas Sandora School Based Study of Elementary School Classrooms The Clorox Company
Sam Nurko A Pilot Study of Miralax Syrup in Constipated Children Braintree Labs
Sam Nurko Pantoprazole Wyeth
Lynda Schneider Study of CE1145 in Subjects with Congenital C1-INH Deficiency and Acute HAE Attacks ZLB Behring
Rosalind Brown Growth Failure Associated with Primary IGF-1 Deficiency Tercica, Inc.
Anne Fulton Clinical Study AK15 Entitled ''Effect of Supplemented Infant Formula on Blood Levels in Preterm Infants.'' Abbott Ross Laboratories
Lynda Schneider APPLES: A Prospective Pediatric Evaluation of Tacrolimus Ointment for Treatment of Atopic Dermatitis Astellas Pharma US, Inc.
Mary McCann Study To Evaluate the Correlation of the SEDLine PSI with End-Tidal Sevoflurane Concentration in a Pediatric Patient Population. Hospira Sedation, Inc.
Neil Feins Minimal Invasive Closure, M.I.C., Using an Available Bovine Collagen Injection to Close Hernias Q-Med, Inc.
Jane Newburger Cardiolite Bristol Myers Squibb
Sam Nurko Pantoprazole Wyeth
Sam Nurko Pantoprazole Wyeth
Mark Waltzman Clinical Trial Investigation Use of Dextrose Containing Fluids In Abbott Diabetes Care
Charles Berul Pediatric ICD Lead Evaluation Study Medtronic, Inc. and Guidant
Maureen Jonas Comparison of FibroScan and Serum Fibrosis Markers in Pediatric Patients Presenting for Liver Biopsy Beth Israel Deaconess Medical Center
Rosalind Brown Int'l Growth Hormone Study Pfizer, Inc.
Rosalind Brown The Growth Hormone Monitor Serono
Sandra Burchett TMC114/rtcv b.i.d. in Children With H.I.V. Tibotec Pharmaceuticals Ltd.
William Harmon Safety and Efficacy of Three Venofer Iron Maintenance Regimens in Pediatric Dialysis Dependent Chronic Kidney Disease Patients Luitpold Pharmaceuticals
Alison Rentz Trial to Assess Safety of the Antiseptic Chlorhexidine Gluconate in Neonatal Patients with Central Venous Catheters MediFlex Surgical Instruments
Jonathan Mansbach Children of Low Socio-Economic Status (SES) Children are Not Receiving Synagis. MedImmune, Inc.
Francisco Bonilla Association of Anti-IgA Antibodies with Adverse Ractions to Gamma Globulin Infusion Talecris Biotherapeutics
Children's HospitalTerms and Conditions
Site Designed and Developed by Genuine