Clinical Trials
Clinical Trials at Children's
Children's Hospital Boston houses 225 specialty clinics, each of which could be a potential clinical trial site. Children’s Hospital Boston has long been a major site for clinical trials in a number of areas, including muscular dystrophy, through our Neuromuscular Program, Cystic Fibrosis, through our CF Center, and metabolic disorders. More recently, we have launched clinics in Fragile X, Tuberous Sclerosis and Rett Syndrome, rapidly bringing together the patient population and clinical trial infrastructure needed when a laboratory discovery leads to the suggestion of a trial in clinic that could help our patients. Since many of our clinicians are also researchers, many of our INDs are physician-sponsored.
As a leading academic research hospital, Children's is also a pioneer in developing cutting-edge treatment modalities for the rarest of disorders. For example, in 2010, Children’s took the lead in launching the first gene therapy trial in the United States in over a decade to treat children with X-linked severe combined immunodeficiency (SCID-X1).
For more information about performing clinical research with a Children’s Hospital clinician, contact TIDO at (617) 919-3019, ext. 43019 or email TIDO@childrens.harvard.edu.